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FDA approves Ionis, AZ’s Wainua for ATTR polyneuropathy

AstraZeneca and Ionis are planning a US launch next month for Wainua, their treatment for polyneuropathy in life-threatening disease transthyretin-mediated amyloidosis (AT

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Alnylam’s expansion plan for Onpattro blocked by FDA

Alnylam has abandoned plans to add cardiomyopathy to the label for transthyretin-mediated amyloidosis (ATTR) therapy Onpattro after the FDA turned down its marketing appli

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Alnylam's Onpattro clears FDA vote for ATTR-cardiomyopathy

Despite a sceptical appraisal by FDA reviewers, Alnylam's Onpattro has been recommended for approval as a treatment for transthyretin amyloidosis cardiomyopathy (ATTR-CM)

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BridgeBio rebounds on ATTR cardiomyopathy data

BridgeBio is getting ready to file for FDA approval of its acoramidis drug for transthyretin amyloidosis (ATTR) cardiomyopathy, armed with positive results in a phase 3 tr

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Alnylam grabs FDA approval for its second amyloidosis therap...

Four years after getting the first drug approved by the FDA to treat rare disease hereditary ATTR amyloidosis, Alnylam has got the go-ahead for a second – Amvuttra – which has a simpler, mo

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West Chester - Circa November 2020: AstraZeneca plant. AstraZeneca has been working on a vaccine for the Coronavirus, COVID and COVID-19.

AstraZeneca goes bigger in amyloidosis with Neurimmune deal

AstraZeneca has clearly made the rare disease transthyretin amyloidosis (ATTR) a key component of its rare disease pipeline, licensing a second drug candidate in the space of a couple of mo

FDA approves Ionis, AZ’s Wainua for ATTR polyneuropathy

Alnylam’s expansion plan for Onpattro blocked by FDA

Alnylam's Onpattro clears FDA vote for ATTR-cardiomyopathy

BridgeBio rebounds on ATTR cardiomyopathy data

Alnylam grabs FDA approval for its second amyloidosis therap...

AstraZeneca goes bigger in amyloidosis with Neurimmune deal

Gene therapy firm Kate Tx snapped up by Novartis for $1.1bn

Coming soon: The Life Sciences Industry Report 2025 – insigh...

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