
X
Girl loses High Court battle over NICE review of BioMarin’s PKU drug
https://pharmaphorum.com/news/girl-loses-high-court-battle-over-nice-review-of-biomarins-pku-drug/
Project will initially focus on DMD but could benefit other rare diseases
A new way to capture when drugs are ‘cost effective’ but not ‘affordable’ looks set to be introduced in England.
Leela Barham examines the process for the appraisal of Highly Specialised Technologies.