gene therapy

News

Sanofi winds $40m into UK gene therapy firm Gyroscope

French drugmaker Sanofi has made a $40 million investment in Gyroscope Therapeutics, with another $20 million potentially on offer as the UK biotech advances its clinical-stage gene therapi

News

Astellas reports fourth death in halted gene therapy trial

There has been a fourth patient fatality in Astellas' clinical trial of its AT132 gene therapy for the rare disease X-linked myotubular myopathy (XLMTM), which has been halted twice due to

News

AbbVie spies potential in Regenxbio eye disease gene therapy

AbbVie has expanded its ophthalmology pipeline via a licensing deal with Regenxbio, paying $370 million upfront to get its hands on a gene therapy for wet age-related macular degeneration (

News

DNA helix in a futuristic concept of the evolution of science and medicine.

FDA slaps clinical hold on BioMarin's PKU gene therapy

BioMarin Pharma has had another setback in its gene therapy development programme, announcing this morning that the FDA has placed a phase 1/2 trial of its candidate for phenylketonuria (PK

News

More trouble for Astellas as AT132 gene therapy trial is hal...

Astellas has halted dosing in a study of its AT132 gene therapy for the rare disease X-linked myotubular myopathy (XLMTM) for the second time after another serious adverse event (SAE) linke

News

Gene therapy specialist bluebird exits "untenable" European ...

Europe's market has proved so hostile to gene therapies when it comes to pricing and reimbursement for gene therapies that bluebird bio has decided to quit the market altogether, according

Sanofi winds $40m into UK gene therapy firm Gyroscope

Astellas reports fourth death in halted gene therapy trial

AbbVie spies potential in Regenxbio eye disease gene therapy

FDA slaps clinical hold on BioMarin's PKU gene therapy

More trouble for Astellas as AT132 gene therapy trial is hal...

Gene therapy specialist bluebird exits "untenable" European ...

Study finds AZ's benralizumab a 'game-changer' in asthma

Coming soon: The Life Sciences Industry Report 2025 – insigh...

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