gene therapy

News

SparingVision raises €75m for eye disease gene therapies

SparingVision has raised €75 million in second-round funding that will be used to fund clinical trials of gene therapies for ocular diseases retinitis pigmentosa (RP) and dry age-related ma

R&D

Automation in the clinical laboratory. Pipetting robot laboratory. Medicine robotics. Research and science background

Expectations rise for gene therapy to change treatment lands...

After a recent approval, there are now three gene therapies available on the US market.

News

Roctavian okay sets up another gene therapy test for Europe

BioMarin Pharma has its landmark first approval for Roctavian – the first for a haemophilia gene therapy – and will now have to see if that can convert that into a viable business in Europe

News

DNA helix in a futuristic concept of the evolution of science and medicine.

Bayer unit BrainVectis cleared to start Huntington gene ther...

France's BrainVectis, a subsidiary of Bayer's Asklepios BioPharma (AskBio) unit, has been given the green light by regulators in France to start dosing patients with its gene therapy candid

News

bluebird unveils $2.8m price for gene therapy Zynteglo on FD...

bluebird bio's Zynteglo has become the first cell-based gene therapy to be approved in the US, getting the nod from the FDA as a treatment for patients with beta thalassaemia who require re

News

Young lonely man in a wheelchair on a balcony looking at the nature in the spring

Sarepta says early filing for DMD gene therapy is back on

Sarepta is pressing forward with a bold plan to file with the FDA for accelerated approval of its gene therapy SRP-9001 for Duchenne muscular dystrophy (DMD) in the next few months, with a

SparingVision raises €75m for eye disease gene therapies

Expectations rise for gene therapy to change treatment lands...

Roctavian okay sets up another gene therapy test for Europe

Bayer unit BrainVectis cleared to start Huntington gene ther...

bluebird unveils $2.8m price for gene therapy Zynteglo on FD...

Sarepta says early filing for DMD gene therapy is back on

Lily gets FDA nod for SERD-CDK 4/6 combo in breast cancer

Discover a new era of healthcare panel engagement: Grounded ...

gene therapy

Editor's Picks