R&D Strength in numbers: Because having a rare disease isn’t rar... Rare doesn’t mean insignificant – in fact more people live with a rare disease than with cancer and AIDS combined.
R&D The patient perspective on advocacy Growing up with the shadow of Huntington’s disease (HD) means Seth Rotberg understands the importance of peer support and credible information.
R&D How pharma can support doctors who treat rare diseases Where do doctors see patients with rare diseases, how do they keep up with treatment advances and what can pharmaceutical companies do to help?
R&D Living with LHON: Adapting to sight loss at 15 years old When faced with a devastating diagnosis, a family has two choices – to give up or make it their mission to adapt and carry on.
R&D A lifeline for rare disease patients For more than 25 years Alexion has been blazing a trail in rare diseases, bringing a series of life-changing medicines to market.
R&D Realising the potential of wearable tech Spire Health, a US-based continuous respiration sensing and high-adherence ambulatory monitoring healthcare company, is poised to revolutionise the wearable tech space for use in clinical s
News Neurogene drops high-dose arm in Rett study after death The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died
Sales & Marketing Coming soon: The Life Sciences Industry Report 2025 – insigh... Prepare for 2025 with pharmaphorum’s Life Sciences Report, featuring expert insights on AI in drug development, gene therapy, and top industry trends
