BioMarin | pharmaphorum

Friday 22 November 2024

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BioMarin

News

nektar_sign-san_francisco

Nektar, BioMarin, and Alnylam top list of biotech M&A target...

With Takeda’s £46 billion acquisition of Shire, it’s been a busy year for pharma M&A – and according to analysts Datamonitor, the specialist biotechs Nektar, BioMarin and Alnylam are th

News

NICE1

NICE rejects Biomarin's £520K per year rare disease drug

Company will negotiate access scheme

News

atlanta_georgia

‘Cure for hemophilia within reach’ as BioMarin and Spark gen...

While clinicians attending the American Society of Hematology meeting in Atlanta this weekend were anticipating a flurry of exciting data, the conference wasn’t entirely prepared for the ac

News

Breakthrough status for BioMarin ratchets up haemophilia A competition

Breakthrough status for BioMarin ratchets up haemophilia A c...

The FDA has granted Breakthrough Therapy Designation to BioMarin’s gene therapy for haemophilia A, helping to intensify competition in the field.

News

EU regulators back two more orphan drugs, question of pricin...

Two orphan medicines are heading towards the European market, after regulators recommended rare disease drugs from Biogen and BioMarin.

News

DNA sequence

New NICE rules could deny drugs to rare disease patients

Patients could be denied treatments, says BIA