ataxia

News

PTC slides on failed Friedreich ataxia study

PTC Therapeutics has cued up no fewer than three clinical trial readouts this quarter that could lead to new regulatory filings – but the latest for vatiquinone in inherit

News

Healx deploys its AI in hunt for Friedreich's ataxia therapi...

UK artificial intelligence specialist Healx has begun a partnership with two medical charities that aims to uncover new therapies for the neurodegenerative disease Friedreich's ataxia (FA).

Digital

Interview at Hlth 2025 with Dr Adam Brow

Chaos & opportunity: Dr Adam Brown unpacks US health policy

Dive into our video interview with Dr Adam Brown as he unpacks the chaos and opportunity shaping US health policy.

Market Access

pharmaphorum podcast Episode 178a - Sandra Anderson and Chris Williams, Cencora

The value of a partner, globally and locally

A new podcast looks at recent trends related to drug approvals, as well as challenges and opportunities both small and large pharma companies face

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