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Data backs AZ’s Wilson disease drug, but with a question mark

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AADC deficiency

Genetic engineeering concept

Market Access/ News/ News

PTC gets green light for gene therapy Upstaza in EU

Phil Taylor AADC deficiency, CHMP, EU, gene therapy, PTC Therapeutics, rare disease, Upstaza 0 Comment

PTC Therapeutic’s Upstaza gene therapy for patients with genetic disorder AADC deficiency has been recommended for approval in

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PTC gets green light for gene therapy Upstaza in EU

https://pharmaphorum.com/news/ptc-gets-green-light-for-gene-therapy-upstaza-in-eu/

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Biogen and Happify partner on digital support for MS patients
Data backs AZ's Wilson disease drug, but with a question mark
GSK pledges £1bn drive for infectious disease R&D
Fujifilm acquires AI tech to improve fertility treatment
Sarepta shares yo-yo as FDA places hold on Duchenne trial

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