Rare Disease

R&D
Amplifying the voices in rare diseases

Amplifying the voices in rare diseases

There are approximately 300 million people around the world living with a rare disease. Yet, until relatively recently, there was limited focus on this heterogenous population.

News
Joe Wiley, chief executive, Amryt_Pharma

FDA turns down Amryt's epidermolysis bullosa drug

Amryt Pharma has been handed a major blow by the FDA, after the US regulator rejected its marketing application for Oleogel-S10, its drug for rare and debilitating skin disease epidermolysi