Rare disease drug Strensiq too expensive, says NICEAlexion’s new rare disease treatment Strensiq has been rejected by England’s health watchdog NICE in draft guidance. Strensiq Share XRare disease drug Strensiq too expensive, says NICEhttps://pharmaphorum.com/news/rare-disease-drug-strensiq-too-expensive-says-nice/
Rare disease drug Vimizim gets NICE ‘yes’ – but needs real-world dataNICE says it can approve BioMarin’s ultra-rare drug treatment Vimizim, but has proposed real-world data collection and a Share XRare disease drug Vimizim gets NICE ‘yes’ – but needs real-world datahttps://pharmaphorum.com/views-and-analysis/rare-disease-drug-vimizim-gets-nice-yes/