thalassaemia

News

Editas axes two-thirds of its staff, including its CMO

Editas Medicine ends development of its gene-editing therapy for thalassaemia and sickle cell, shedding 65% of staff and narrowing its R&D focus.

News

FDA sets Dec deadline for Vertex, CRISPR sickle cell therapy

The FDA has started a priority review of Vertex Pharma and CRISPR Therapeutics’ exagamglogene autotemcel (exa-cel) in sickle cell disease (SCD), with a decision on approva

News

First human trials of lab-grown red blood cells start in UK

Blood cells grown in a laboratory have been given to people for the first time in a clinical trial being carried out by researchers in the UK, in the hope that plentiful supplies of rare bl

News

Novo Nordisk steps up sickle cell push with $1.1bn Forma buy

Novo Nordisk has doubled down on position in the sickle cell disease (SCD) category with a $1.1 billion agreement to acquire Forma Therapeutics, and its therapeutic candidate etavopivat, in

News

Parliamentary probe finds racism evidence in NHS sickle cell...

Patients with sickle cell disease are facing racism in the NHS that is putting their lives a risk, claims a new report.

News

Silence Tx uses game to raise thalassaemia awareness

UK biotech Silence Therapeutics has launched an online game to raise the profile of the rare blood disorder thalassaemia, and one of its most common symptoms.

Editas axes two-thirds of its staff, including its CMO

FDA sets Dec deadline for Vertex, CRISPR sickle cell therapy

First human trials of lab-grown red blood cells start in UK

Novo Nordisk steps up sickle cell push with $1.1bn Forma buy

Parliamentary probe finds racism evidence in NHS sickle cell...

Silence Tx uses game to raise thalassaemia awareness

World Without Disease initiative: 2024 update

The AI effect in pharma commercial strategy: From data to re...

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