sickle cell disease

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Professor Bola Owolabi, director of the National Healthcare Inequalities Improvement Programme at NHS England

Winners named in NHS healthcare inequality contest

A competition aimed at tackling unequal access to healthcare in the NHS has been won by C2-Ai, a company that has developed an artificial intelligence-based risk assessmen

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CHMP backs Biogen’s Skyclarys for Friedreich’s ataxia

Biogen’s Skyclarys is on course to becoming the first approved medicine for the inherited neurological disease Friedreich’s ataxia (FA) in the EU after it was recommended

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Vertex Pharmaceutical's Boston headquarters

FDA clears two sickle-cell gene therapies, including CRISPR ...

The US FDA has cleared two novel gene therapies for sickle cell disease: Vertex Pharmaceuticals' Casgevy and bluebird bio's Lyfgenia.

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UK first to approve Vertex, CRISPR drug for blood disorders

The first-ever CRISPR-based gene-editing therapy has been approved for marketing in the UK for inherited blood disorders sickle cell disease (SCD) and transfusion-dependen

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FDA sets Dec deadline for Vertex, CRISPR sickle cell therapy

The FDA has started a priority review of Vertex Pharma and CRISPR Therapeutics’ exagamglogene autotemcel (exa-cel) in sickle cell disease (SCD), with a decision on approva

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EU approval for Novartis’ sickle cell drug set to be pulled

Novartis has said it is “disappointed” that the EMA’s Human Medicines Committee has recommended revoking the conditional EU approval for sickle cell disease (SCD) therapy

Winners named in NHS healthcare inequality contest

CHMP backs Biogen’s Skyclarys for Friedreich’s ataxia

FDA clears two sickle-cell gene therapies, including CRISPR ...

UK first to approve Vertex, CRISPR drug for blood disorders

FDA sets Dec deadline for Vertex, CRISPR sickle cell therapy

EU approval for Novartis’ sickle cell drug set to be pulled

Roche gets EU okay for chest pain algorithm

Health Trends 2025: Reimagining What's Possible

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