sickle cell disease

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Sickle cell gene therapy Casgevy finally cleared for NHS use

Vertex's gene-editing therapy for sickle cell disease, Casgevy, has been given the nod for use by the NHS in England after an earlier rejection.

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Editas axes two-thirds of its staff, including its CMO

Editas Medicine ends development of its gene-editing therapy for thalassaemia and sickle cell, shedding 65% of staff and narrowing its R&D focus.

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Beam Therapeutics' chief executive John Evans

Beam points to positive data with key base editing asset

It has been around a year since Beam Therapeutics slashed its headcount and R&D programmes to focus mainly on a sickle cell disease candidate – and the biotech has now revealed the firs

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Pfizer pulls sickle cell med Oxbryta off market after deaths

Pfizer is voluntarily withdrawing its sickle cell disease (SCD) therapy Oxbryta from all world markets after finding an "imbalance" in deaths in its clinical trials programme.

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After a no in sickle cell, NICE OKs Casgevy for thalassaemia

Vertex and CRISPR Therapeutics have won the backing of NICE for their gene-editing therapy Casgevy as a treatment for the blood disorder beta thalassaemia, a few months after turning it dow

News

Price cut unlocks NHS use of sickle cell drug Oxbryta

It has been nearly two years since Pfizer’s sickle cell disease (SCD) therapy Oxbryta was approved in the UK, but patients will now be able to access the treatment after a

Sickle cell gene therapy Casgevy finally cleared for NHS use

Editas axes two-thirds of its staff, including its CMO

Beam points to positive data with key base editing asset

Pfizer pulls sickle cell med Oxbryta off market after deaths

After a no in sickle cell, NICE OKs Casgevy for thalassaemia

Price cut unlocks NHS use of sickle cell drug Oxbryta

Prevention for a healthier, more productive society

Health Trends 2025: Reimagining What's Possible

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sickle cell disease

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