sickle cell disease

News

Editas axes two-thirds of its staff, including its CMO

Editas Medicine ends development of its gene-editing therapy for thalassaemia and sickle cell, shedding 65% of staff and narrowing its R&D focus.

News

Beam Therapeutics' chief executive John Evans

Beam points to positive data with key base editing asset

It has been around a year since Beam Therapeutics slashed its headcount and R&D programmes to focus mainly on a sickle cell disease candidate – and the biotech has now revealed the firs

News

Pfizer pulls sickle cell med Oxbryta off market after deaths

Pfizer is voluntarily withdrawing its sickle cell disease (SCD) therapy Oxbryta from all world markets after finding an "imbalance" in deaths in its clinical trials programme.

News

After a no in sickle cell, NICE OKs Casgevy for thalassaemia

Vertex and CRISPR Therapeutics have won the backing of NICE for their gene-editing therapy Casgevy as a treatment for the blood disorder beta thalassaemia, a few months after turning it dow

News

Price cut unlocks NHS use of sickle cell drug Oxbryta

It has been nearly two years since Pfizer’s sickle cell disease (SCD) therapy Oxbryta was approved in the UK, but patients will now be able to access the treatment after a

News

Professor Bola Owolabi, director of the National Healthcare Inequalities Improvement Programme at NHS England

Winners named in NHS healthcare inequality contest

A competition aimed at tackling unequal access to healthcare in the NHS has been won by C2-Ai, a company that has developed an artificial intelligence-based risk assessmen

Editas axes two-thirds of its staff, including its CMO

Beam points to positive data with key base editing asset

Pfizer pulls sickle cell med Oxbryta off market after deaths

After a no in sickle cell, NICE OKs Casgevy for thalassaemia

Price cut unlocks NHS use of sickle cell drug Oxbryta

Winners named in NHS healthcare inequality contest

Life Sciences Industry Report – Part 3

Health Trends 2025: Reimagining What's Possible

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