Sarepta

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Surfing on new Duchenne data, Wave charges $175m offering

Phase 2 results with Wave Life Sciences' Duchenne muscular dystrophy candidate WVE-N531 pushed the company's share price to its highest level in a year and could lead to discussions with re

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Sarepta bags key expansion to DMD gene therapy label in US

Sarepta’s gene therapy for Duchenne muscular dystrophy (DMD) will be an option for many more patients in the US after the FDA expanded the breadth of its approved labelling.

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Future of Pfizer’s Duchenne gene therapy in doubt

Pfizer is “evaluating appropriate next steps” for its Duchenne muscular dystrophy (DMD) gene therapy after it failed a phase 3 trial.

News

Despite trial miss, Sarepta plans new filing for DMD therapy

Sarepta Therapeutics’ gene therapy for Duchenne muscular dystrophy has failed to meet its primary objective in a phase 3 trial, but the company says it will file to extend

News

Big day for Duchenne as Sarepta gets first gene therapy nod

Almost against the odds, Sarepta’s gene therapy for muscle-wasting disease Duchenne muscular dystrophy (DMD) has been given accelerated approval by the FDA, albeit in a fa

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FDA advisors narrowly back Sarepta’s Duchenne gene therapy

An FDA advisory committee has given tentative backing to Sarepta’s gene therapy for Duchenne muscular dystrophy (DMD), even though the agency’s reviewers said they were no

Surfing on new Duchenne data, Wave charges $175m offering

Sarepta bags key expansion to DMD gene therapy label in US

Future of Pfizer’s Duchenne gene therapy in doubt

Despite trial miss, Sarepta plans new filing for DMD therapy

Big day for Duchenne as Sarepta gets first gene therapy nod

FDA advisors narrowly back Sarepta’s Duchenne gene therapy

Incyte blocks US launch of Sun Pharma's alopecia drug

Global reach, personal touch: Mastering customer engagement ...

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