Sarepta

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Sarepta pulls plug on Duchenne exon-skipping drug

Sarepta Therapeutics has decided not to continue the development of vesleteplirsen, a follow-up to its Duchenne muscular dystrophy (DMD) therapy Exondys 51.

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Surfing on new Duchenne data, Wave charges $175m offering

Phase 2 results with Wave Life Sciences' Duchenne muscular dystrophy candidate WVE-N531 pushed the company's share price to its highest level in a year and could lead to discussions with re

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Sarepta bags key expansion to DMD gene therapy label in US

Sarepta’s gene therapy for Duchenne muscular dystrophy (DMD) will be an option for many more patients in the US after the FDA expanded the breadth of its approved labelling.

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Future of Pfizer’s Duchenne gene therapy in doubt

Pfizer is “evaluating appropriate next steps” for its Duchenne muscular dystrophy (DMD) gene therapy after it failed a phase 3 trial.

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Despite trial miss, Sarepta plans new filing for DMD therapy

Sarepta Therapeutics’ gene therapy for Duchenne muscular dystrophy has failed to meet its primary objective in a phase 3 trial, but the company says it will file to extend

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Big day for Duchenne as Sarepta gets first gene therapy nod

Almost against the odds, Sarepta’s gene therapy for muscle-wasting disease Duchenne muscular dystrophy (DMD) has been given accelerated approval by the FDA, albeit in a fa

Sarepta pulls plug on Duchenne exon-skipping drug

Surfing on new Duchenne data, Wave charges $175m offering

Sarepta bags key expansion to DMD gene therapy label in US

Future of Pfizer’s Duchenne gene therapy in doubt

Despite trial miss, Sarepta plans new filing for DMD therapy

Big day for Duchenne as Sarepta gets first gene therapy nod

PBM reform dropped in Congress' funding package

The AI effect in pharma commercial strategy: From data to re...

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