Sarepta

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DMD gene therapy Elevidys linked to new liver failure case

Another death from liver failure has been seen with Roche and Sarepta's Duchenne muscular dystrophy therapy Elevidys, prompting a pause on treatment.

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Multiple studies of Sarepta's DMD therapy halted after death

Three studies of Sarepta's Elevidys Duchenne gene therapy have been placed on hold as the death of a 16-year-old boy is investigated.

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Sarepta slumps on Elevidys patient death

The death of a patient treated with Sarepta's Duchenne muscular dystrophy gene therapy Elevidys has hit its share price.

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Sarepta pulls plug on Duchenne exon-skipping drug

Sarepta Therapeutics has decided not to continue the development of vesleteplirsen, a follow-up to its Duchenne muscular dystrophy (DMD) therapy Exondys 51.

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Surfing on new Duchenne data, Wave charges $175m offering

Phase 2 results with Wave Life Sciences' Duchenne muscular dystrophy candidate WVE-N531 pushed the company's share price to its highest level in a year and could lead to discussions with re

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Sarepta bags key expansion to DMD gene therapy label in US

Sarepta’s gene therapy for Duchenne muscular dystrophy (DMD) will be an option for many more patients in the US after the FDA expanded the breadth of its approved labelling.

DMD gene therapy Elevidys linked to new liver failure case

Multiple studies of Sarepta's DMD therapy halted after death

Sarepta slumps on Elevidys patient death

Sarepta pulls plug on Duchenne exon-skipping drug

Surfing on new Duchenne data, Wave charges $175m offering

Sarepta bags key expansion to DMD gene therapy label in US

Merck and oncology: A conversation with Dr Gregory Lubinieck...

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