Roctavian

News

BioMarin gets first access deal in EU for gene therapy Rocta...

BioMarin's has signed the first contract with an insurer in Germany for Roctavian, its recently approved gene therapy for haemophilia A, as it tests out its outcomes-based agreement (OBA) r

News

Roctavian okay sets up another gene therapy test for Europe

BioMarin Pharma has its landmark first approval for Roctavian – the first for a haemophilia gene therapy – and will now have to see if that can convert that into a viable business in Europe

News

BioMarin gene therapy for haemophilia on course for EU appro...

The EMA's human medicines advisory committee has recommended that BioMarin Pharmaceutical's haemophilia A gene therapy Roctavian be approved in the EU, removing one of the last barriers to

BioMarin gets first access deal in EU for gene therapy Rocta...

Roctavian okay sets up another gene therapy test for Europe

BioMarin gene therapy for haemophilia on course for EU appro...

Sanofi drops BTK drug tolebrutinib in myasthenia gravis

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