Following yesterday’s international Rare Disease Day, here is a snapshot of four new rare disease treatments currently under review by England’s cost-effectiveness watchdog.
The FDA has marked today’s international Rare Disease Day with a number of measures to promote research and patient participation in policy and research.
Pharma company Shire and tech giant Microsoft are to team up with Eurodis, a not-for-profit group representing 700 rare disease organisations, with the goal of cutting the long wait most patients with rare conditions endure before diagnosis.
A pharma company’s core mission is to improve patient outcomes. This hinges on effectively influencing HCP clinical behaviour and driving disease education.
