Rare diseases

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Bringing gene therapies to market

Bringing gene therapies to market

Doug Danison, vice-president, head of access, value and evidence strategy at bluebird bio, a gene therapy company, looks at the obstacles, opportunities and required change in thinking need

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engineering and genetic editing through the Crispr technique. DNA chain breaking down. 3D rendering

Amicus expands gene therapy collaboration

Amicus Therapeutics and the Perelman School of Medicine at the University of Pennsylvania have announced a major expansion to their R&D collaboration for gene therapies.