Patients Caring for rare: Celebrating Rare Disease Day 2023 Rare Disease Day is observed annually on what is considered the rarest day of the year.
R&D Rare Disease R&D: one step forward, but a long road ahead With over 40% of all medicines in the pipeline aimed at rare diseases, the future looks positive for increasing the number of treatments available.
News Rare diseases have tenfold higher impact on healthcare costs... A new study has suggested that the economic burden posed by rare diseases is around 10 times higher than for common "mass market" conditions.
Views & Analysis Why we need research into the mental health impact of a rare... Rare diseases impact between 3.5%-5.9% of the world’s population.
Views & Analysis Expediting innovation in the rare disease domain Rare diseases affect a fraction of the population – 450 million+ peop
Views & Analysis Rare disease insights from the patient community To help pharma companies understand what life is really like for patients with a rare disease, a new resource has been released to coincide with Rare Disease Day 2021.
News Gene therapy firm Kate Tx snapped up by Novartis for $1.1bn Novartis buys gene therapy specialist Kate Therapeutics for $1.1 billion, adding an early-stage rival to Sarepta's muscular dystrophy therapy Elevidys
Sales & Marketing Coming soon: The Life Sciences Industry Report 2025 – insigh... Prepare for 2025 with pharmaphorum’s Life Sciences Report, featuring expert insights on AI in drug development, gene therapy, and top industry trends
