Rare Disease Day Archives -

A new study has suggested that the economic burden posed by rare diseases is around 10 times higher

Rare diseases have tenfold higher impact on healthcare costs; study

https://pharmaphorum.com/news/rare-diseases-have-tenfold-higher-impact-on-healthcare-costs-study/

R&D/ Views & Analysis/ Views and analysis

Rare Disease R&D: one step forward, but a long road ahead

Ben Hargreaves Rare Disease Day, rare disease R&D, Rare diseases 0 Comment

With over 40% of all medicines in the pipeline aimed at rare diseases, the future looks positive for

Rare Disease R&D: one step forward, but a long road ahead

https://pharmaphorum.com/r-d/rare-disease-rd-one-step-forward-but-a-long-road-ahead/

Expediting Innovations in Rare Disease Domain

R&D/ Views & Analysis/ Views and analysis

Expediting innovation in the rare disease domain

mike.hammerton@pharmaphorum.com Innovation, rare disease, Rare Disease Day 0 Comment

Rare diseases affect a fraction of the population – 450 million+ people globally. However, its effects can be

Expediting innovation in the rare disease domain

https://pharmaphorum.com/r-d/views-analysis-r-d/expediting-innovations-in-rare-disease-domain/

Why research into the mental health impact of a rare disease diagnosis is long overdue

R&D/ Views & Analysis/ Views and analysis

Why we need research into the mental health impact of a rare disease diagnosis

mike.hammerton@pharmaphorum.com mental health, Rare Disease Day, Rare diseases 0 Comment

Rare diseases impact between 3.5%-5.9% of the world’s population. For Rare Disease Day, RBW Consulting’s Emma Thorp discusses

Why we need research into the mental health impact of a rare disease diagnosis

https://pharmaphorum.com/views-and-analysis/the-mental-health-impact-of-a-rare-disease-diagnosis/

Patients/ Views & Analysis/ Views and analysis

Building a better future for people with rare diseases in all four UK nations

Amanda Barrell Genetic Alliance UK, Rare Disease Day, rare disease framework, Rare diseases, UK government 0 Comment

How has rare disease care changed over the last few years? And what might we expect from the

Building a better future for people with rare diseases in all four UK nations

https://pharmaphorum.com/views-analysis-patients/building-a-better-future-for-people-with-rare-diseases-in-all-four-uk-nations/

R&D/ Views & Analysis/ Views and analysis

Rare disease insights from the patient community

mike.hammerton@pharmaphorum.com Bedrock Healthcare Communications, Cambridge Rare Disease Network, Origins Insights, Rare Disease Day, Rare diseases 0 Comment

To help pharma companies understand what life is really like for patients with a rare disease, a new

Rare disease insights from the patient community

https://pharmaphorum.com/views-and-analysis/rare-disease-insights-from-the-patient-community/

The biggest challenges in rare disease drug development – and how the industry is fighting them

Market Access/ R&D/ Views & Analysis/ Views & Analysis/ Views and analysis

The biggest challenges facing rare disease pharma – and how the industry can tackle them

George Underwood Cambridge Rare Disease Network, orphan drugs, pricing, Rare Disease Day, Rare diseases 0 Comment

As Rare Disease day 2020 approaches, we take a look at the biggest challenges facing orphan drug developers

The biggest challenges facing rare disease pharma – and how the industry can tackle them

https://pharmaphorum.com/r-d/views-analysis-r-d/biggest-challenges-rare-disease/

Molecular, DNA and atom model in science research lab

Market Access/ Patients/ Views & Analysis/ Views & Analysis/ Views and analysis

Rare Disease Day: How the patient voice can tear down barriers

Amanda Barrell access to new medicines, clinical trials, drug development, patient engagement, patient voice, Rare Disease Day, Rare diseases, unmet need 0 Comment

To have any impact, patient engagement needs to start with the drug development pathway, not at the point

Rare Disease Day: How the patient voice can tear down barriers

https://pharmaphorum.com/views-and-analysis/rare-disease-day-how-the-patient-voice-can-tear-down-barriers/

Healthcare/ Market Access/ News/ News/ Top stories/ US

Marking Rare Disease Day, FDA and patient group launch collaboration

Andrew McConaghie fda, NORD, patientcentricity, Rare Disease Day, Rare Disease Day 2018, Rare diseases 0 Comment

The FDA has marked today’s international Rare Disease Day with a number of measures to promote research and

Marking Rare Disease Day, FDA and patient group launch collaboration

https://pharmaphorum.com/news/marking-rare-disease-day-fda-patient-group-launch-collaboration/

Trending

Rare Disease Day

Login