News/ Sales and Marketing/ US Kanuma approval adds to Alexion rare disease roster Andrew McConaghie Alexion, Kanuma, Rare diseases 0 Comment Alexion has gained FDA approval for Kanuma, its treatment for the rare disease lysosomal acid lipase (LAL) deficiency. Alexion Share X Kanuma approval adds to Alexion rare disease roster https://pharmaphorum.com/news/kanuma-approval-adds-to-alexion-rare-disease-roster/