News/ News/ R&D Regenxbio expands MPS I gene therapy trial after first look at data Phil Taylor gene therapy, Hurler syndrome, rare disease, Regenxbio 0 Comment Data from the first patients enrolled into Regenxbio’s trial of its gene therapy for rare inherited disease mucopolysaccharidosis Share X Regenxbio expands MPS I gene therapy trial after first look at data https://pharmaphorum.com/news/regenxbio-expands-mps-i-gene-therapy-trial-after-first-look-at-data/