Hemophilia Archives -

Gene Therapy for Blood Disorders Digital Summit

2nd Gene Therapy for Blood Disorders

https://pharmaphorum.com/events/2nd-gene-therapy-for-blood-disorders/

The FDA has granted Breakthrough Therapy Designation to BioMarin’s gene therapy for haemophilia A, helping to intensify competition

Breakthrough status for BioMarin ratchets up haemophilia A competition

https://pharmaphorum.com/news/breakthrough-status-biomarin-ratchets-haemophilia-competition/

Study of nine patients produce encouraging results

Spark reassures on safety of haemophilia gene therapy

https://pharmaphorum.com/news/spark-reassures-safety-haemophilia-gene-therapy/

Haematology is one of the most exciting areas in drug development today, with waves of new treatments emerging

CAR-Ts to take centre stage at ASH haematology congress

https://pharmaphorum.com/news/car-ts-take-centre-stage-haematology-congress/

Hemophilia