Events Partner Content 2nd Gene Therapy for Blood Disorders Gene Therapy for Blood Disorders Digital Summit
News Breakthrough status for BioMarin ratchets up haemophilia A c... The FDA has granted Breakthrough Therapy Designation to BioMarin’s gene therapy for haemophilia A, helping to intensify competition in the field.
News Spark reassures on safety of haemophilia gene therapy Study of nine patients produce encouraging results
News CAR-Ts to take centre stage at ASH haematology congress Haematology is one of the most exciting areas in drug development today, with waves of new treatments emerging for hard-to-treat diseases.
R&D Reuters Pharma USA 2024 – Meruno Perugini Innovation in pharma comes in many forms, but at the end of the day what the industry cares about is results.
Digital Fixing clinical trial data management It’s 2024, and in most clinical trials, data is still being moved from the EHR to the EDC manually – with employees reading data from one screen and typing it onto another.