gene therapy

News

Young lonely man in a wheelchair on a balcony looking at the nature in the spring

Pfizer pauses Duchenne gene therapy trial after patient deat...

Pfizer has called a halt to a clinical trial of its gene therapy for Duchenne muscular dystrophy as it investigates the unexpected death of a young male patient.

News

Trial sets up filings for uniQure's haemophilia gene therapy

Dutch biotech uniQure and partner CSL Behring are planning to file for approval of their gene therapy for haemophilia B, armed with new trial data that they say answers earlier concerns abo

News

engineering and genetic editing through the Crispr technique. DNA chain breaking down. 3D rendering

Dyno attracts $1.6bn gene therapy deal with Astellas

Astellas has signed another bolt-on deal to build its gene therapy pipeline, agreeing a deal with Dyno Therapeutics to tap into its adeno-associated virus (AAV) vector platform for deliveri

News

Sanofi winds $40m into UK gene therapy firm Gyroscope

French drugmaker Sanofi has made a $40 million investment in Gyroscope Therapeutics, with another $20 million potentially on offer as the UK biotech advances its clinical-stage gene therapi

News

Astellas reports fourth death in halted gene therapy trial

There has been a fourth patient fatality in Astellas' clinical trial of its AT132 gene therapy for the rare disease X-linked myotubular myopathy (XLMTM), which has been halted twice due to

News

AbbVie spies potential in Regenxbio eye disease gene therapy

AbbVie has expanded its ophthalmology pipeline via a licensing deal with Regenxbio, paying $370 million upfront to get its hands on a gene therapy for wet age-related macular degeneration (

Pfizer pauses Duchenne gene therapy trial after patient deat...

Trial sets up filings for uniQure's haemophilia gene therapy

Dyno attracts $1.6bn gene therapy deal with Astellas

Sanofi winds $40m into UK gene therapy firm Gyroscope

Astellas reports fourth death in halted gene therapy trial

AbbVie spies potential in Regenxbio eye disease gene therapy

Lily gets FDA nod for SERD-CDK 4/6 combo in breast cancer

Discover a new era of healthcare panel engagement: Grounded ...

gene therapy

Editor's Picks