Elevidys

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DMD gene therapy Elevidys linked to new liver failure case

Another death from liver failure has been seen with Roche and Sarepta's Duchenne muscular dystrophy therapy Elevidys, prompting a pause on treatment.

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Multiple studies of Sarepta's DMD therapy halted after death

Three studies of Sarepta's Elevidys Duchenne gene therapy have been placed on hold as the death of a 16-year-old boy is investigated.

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Sarepta slumps on Elevidys patient death

The death of a patient treated with Sarepta's Duchenne muscular dystrophy gene therapy Elevidys has hit its share price.

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Sarepta bags key expansion to DMD gene therapy label in US

Sarepta’s gene therapy for Duchenne muscular dystrophy (DMD) will be an option for many more patients in the US after the FDA expanded the breadth of its approved labelling.

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Future of Pfizer’s Duchenne gene therapy in doubt

Pfizer is “evaluating appropriate next steps” for its Duchenne muscular dystrophy (DMD) gene therapy after it failed a phase 3 trial.

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Despite trial miss, Sarepta plans new filing for DMD therapy

Sarepta Therapeutics’ gene therapy for Duchenne muscular dystrophy has failed to meet its primary objective in a phase 3 trial, but the company says it will file to extend

DMD gene therapy Elevidys linked to new liver failure case

Multiple studies of Sarepta's DMD therapy halted after death

Sarepta slumps on Elevidys patient death

Sarepta bags key expansion to DMD gene therapy label in US

Future of Pfizer’s Duchenne gene therapy in doubt

Despite trial miss, Sarepta plans new filing for DMD therapy

Amid sector disruption, biotech must focus on 'fundamentals'...

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