Duchenne muscular dystrophy

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Santhera debuts DMD drug Agamree in Germany

Santhera’s new treatment for Duchenne muscular dystrophy Agamree has been launched in its first market, Germany, following its EU approval last month.

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Despite trial miss, Sarepta plans new filing for DMD therapy

Sarepta Therapeutics’ gene therapy for Duchenne muscular dystrophy has failed to meet its primary objective in a phase 3 trial, but the company says it will file to extend

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Santhera closes on first approval for DMD drug vamorolone

Swiss biotech Santhera is on the brink of its first regulatory approval for Duchenne muscular dystrophy treatment vamorolone, after getting a positive opinion on the drug

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EMA starts review of Italfarmaco's Duchenne drug

Italfarmaco's marketing application for HDAC inhibitor givinostat as a treatment for Duchenne muscular dystrophy (DMD) has been accepted by the EMA, setting up an approval

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FibroGen slumps on second failed DMD study

FibroGen has revealed that a second late-stage clinical trial of Duchenne muscular dystrophy (DMD) therapy pamrevlumab has failed to show efficacy, extending a run of bad

News

EMA backs SV95C as digital primary endpoint for DMD trials

The EMA has endorsed a digital measurement using wearables developed by Sysnav Healthcare as a primary endpoint for use in trials involving patients with Duchenne muscular

Santhera debuts DMD drug Agamree in Germany

Despite trial miss, Sarepta plans new filing for DMD therapy

Santhera closes on first approval for DMD drug vamorolone

EMA starts review of Italfarmaco's Duchenne drug

FibroGen slumps on second failed DMD study

EMA backs SV95C as digital primary endpoint for DMD trials

World Without Disease initiative: 2024 update

The AI effect in pharma commercial strategy: From data to re...

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Duchenne muscular dystrophy

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