News Submission completed, Spark sets sight on first ever US gene... Spark Therapeutics has completed the rolling submission of gene therapy product voretigene neparvovec, for patients with a rare genetic form of blindness.
News Sangamo and new gene therapy partner Pfizer lifted by FDA fa... Sangamo Therapeutics has been granted a fast track designation from the FDA for SB-525, its gene therapy candidate for haemophilia A.
News Tax breaks could nurture UK’s cell and gene therapy manufact... Tax breaks for R&D and innovative manufacturing could be part of life sciences strategy.
News Spark and Pfizer's haemophilia gene therapy gets European PR... Decision based on promising data from ongoing phase 1/2 trial.
News Spark reassures on safety of haemophilia gene therapy Study of nine patients produce encouraging results
News Neurogene drops high-dose arm in Rett study after death The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died
Sales & Marketing Coming soon: The Life Sciences Industry Report 2025 – insigh... Prepare for 2025 with pharmaphorum’s Life Sciences Report, featuring expert insights on AI in drug development, gene therapy, and top industry trends