News Vaderis drug lends hope to patients with bleeding disease HH... A trial of Vaderis' AKT inhibitor engasertib finds it could be the first effective treatment for rare disease hereditary haemorrhagic telangiectasia.
News Grifols files drug for rare bleeding disorder in the US Grifols has filed for FDA approval of its new drug for bleeding disorder acquired fibrinogen deficiency (AFD), aiming for a first-in-class US launch.
News Grifols eyes first place in US fibrinogen concentrate market Grifols is gearing up to file for approval of a drug for rare bleeding disorder acquired fibrinogen deficiency (AFD) that could provide a more reliable and easier treatmen
News Hemab raises $135m for rare bleeding disorder trials Cash will be used to advance drugs for Glanzmann thrombasthenia and von Willebrand disease.
Views & Analysis The unmet needs of bleeding disorder patients Ahead of eyeforpharma Philadelphia 2019, we talk to speaker and haemophilia advocate Michelle Rice about the changing landscape for bleeding disorders
News NHS "isn't delivering equitable care for rare diseases" A Genetic Alliance UK report claims the NHS is failing to meet the needs of many of the 3.5 million people in the country who live with rare diseases.
Sales & Marketing Sponsored Using AI-driven synthetic personas to take your insights fur... As AI continues to reshape the healthcare landscape, pharma teams are beginning to leverage synthetic personas.