BioMarin Pharmaceuticals

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BioMarin’s Voxzogo shows promise in hypochondroplasia

BioMarin’s Voxzogo has been shown to increase growth rates in children with hypochondroplasia, a genetic cause of very short stature, in a phase 2 trial.

News

Activist investor Elliott turns its attention to BioMarin

Hedge Fund Elliott Management has bought a big stake in BioMarin Pharma, causing a spike in the company’s share price, and started discussions with the company about its s

News

Change at the top at BioMarin as CEO Bienaimé steps down

After 18 years in charge, BioMarin Pharma’s chief executive and chairman, Jean-Jacques Bienaimé, has announced his retirement, with a high-powered replacement already line

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BioMarin’s haemophilia A gene therapy gets US approval

The FDA has approved BioMarin Pharma’s Roctavian as the first gene therapy for haemophilia A, giving patients an alternative to regular injections of blood clotting factor

News

BioMarin gets first access deal in EU for gene therapy Rocta...

BioMarin's has signed the first contract with an insurer in Germany for Roctavian, its recently approved gene therapy for haemophilia A, as it tests out its outcomes-based agreement (OBA) r

News

Pfizer, Sangamo resume haemophilia gene therapy trial

Pfizer and Sangamo have restarted recruitment of patients into their registration trial for haemophilia A gene therapy giroctocogene fitelparvovec, after the FDA lifted a clinical hold on t

BioMarin’s Voxzogo shows promise in hypochondroplasia

Activist investor Elliott turns its attention to BioMarin

Change at the top at BioMarin as CEO Bienaimé steps down

BioMarin’s haemophilia A gene therapy gets US approval

BioMarin gets first access deal in EU for gene therapy Rocta...

Pfizer, Sangamo resume haemophilia gene therapy trial

‘Insulin for muscle’ and the AI platform behind it, with Han...

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BioMarin Pharmaceuticals

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