ATTR amyloidosis

News

NICE backs Alnylam's Amvuttra for rare form of amyloidosis

Alnylam's gene-silencing drug Amvuttra has been recommended as a treatment for hereditary transthyretin-related (ATTR) amyloidosis by NICE, paving the way for the drug to be made available

News

AstraZeneca goes bigger in amyloidosis with Neurimmune deal

AstraZeneca has clearly made the rare disease transthyretin amyloidosis (ATTR) a key component of its rare disease pipeline, licensing a second drug candidate in the space of a couple of mo

News

AZ gets closer to Ionis, licensing amyloidosis drug in $3.6b...

AstraZeneca has snapped up another Ionis-discovered drug for its pipeline, this time phase 3 candidate eplontersen for the disease transthyretin amyloidosis (ATTR).

News

Alnylam launches digital tool for ATTR amyloidosis patients

Alnylam has been a pioneer in hereditary ATTR amyloidosis, getting approval in 2018 for the first drug to treat the rare disease, and has now launched a digital companion to help patients t

News

Novo Nordisk bulks up in rare diseases with $1.2bn Prothena ...

Diabetes giant Novo Nordisk has opened a new front in its rare disease R&D, thanks to an acquisition agreement with Prothena focusing on drugs for ATTR amyloidosis.

News

Intellia, Regeneron ace first trial with 'in vivo' CRISPR dr...

The first ever clinical data with a CRISPR/Cas9 drug used to edit the genomes of cells within the body has yielded impressive results in patients with ATTR amyloidosis, a life-threatening r

NICE backs Alnylam's Amvuttra for rare form of amyloidosis

AstraZeneca goes bigger in amyloidosis with Neurimmune deal

AZ gets closer to Ionis, licensing amyloidosis drug in $3.6b...

Alnylam launches digital tool for ATTR amyloidosis patients

Novo Nordisk bulks up in rare diseases with $1.2bn Prothena ...

Intellia, Regeneron ace first trial with 'in vivo' CRISPR dr...

Sanofi drops BTK drug tolebrutinib in myasthenia gravis

How Moderna kept diversity in mind amid vaccine development

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ATTR amyloidosis

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