A closer look at gene therapy with PTC Therapeutics
In the latest instalment of the pharmaphorum podcast, editor-in-chief Jonah Comstock connects with Kylie O’Keefe to talk about gene therapy in rare diseases.
They discuss what different gene therapies have in common and how some particular therapies work. They also talk about what gene therapy means for the industry and for patients, in particular the paradigm shift of disease-modifying therapies.
And they look at some of the challenges around cell and gene therapies, including development, commercialisation, and manufacturing challenges, as well as what the next steps are for industry in advancing these therapies.
You can listen to episode 86 of the pharmaphorum podcast in the player below, download the episode to your computer, or find it – and subscribe to the rest of the series in iTunes, Spotify, acast, Stitcher, and Podbean.