Rare Disease

Digital

Eric Luellen and Jonah Comstock interview at AAPS

AI-powered drug discovery is outpacing regulators, with Eric...

During the AAPS National Biotech Conference 2025, pharmaphorum’s Jonah Comstock sat down with Eric Luellen, the founder and CTIO of Turing Biosciences

R&D

Why it is more important than ever to optimise and innovate ...

Rare disease research is vital to improve the lives of hundreds of millions of people worldwide.

R&D

On incentivisation and investment in rare disease R&D

To mark Rare Disease Day, pharmaphorum spoke with Paola Pozzi, partner of telethon strategy at Sofinnova Partners, about the outlook for investment in this field of research.

Digital

Medicine doctor writing electronic medical record

Driving innovation in rare diseases: Digital health and coll...

In recognition of Rare Disease Day, Dr Kamran Iqbal, head of medical affairs and patient advocacy in global rare diseases at Chiesi UK, discussed with pharmaphorum the company’s evolving ro

Market Access

Part Two: Navigating the complexities of global market acces...

The journey to global market access for innovative therapies is fraught with challenges that vary significantly across the world.

Market Access

Part One: Overcoming challenges and seizing opportunities in...

The outlook for drug development to treat rare diseases looks encouraging, offering hope to the 300 million people globally facing the significant challenges of these often-overlooked condi