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Wednesday 29 April 2026

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Tryngolza

News

Sanofi grabs Chinese rights to Arrowhead rare disease drug

Sanofi has paid $130 million upfront for Chinese rights to an Arrowhead Pharma drug for rare disease familial chylomicronaemia syndrome.

News

Lilly's appeal unlocks EU approval of Alzheimer's drug

Lilly's appeal unlocks EU approval of Alzheimer's drug

Eli Lilly's appeal of a decision by the EMA's human medicines committee not to approve its Alzheimer's disease therapy Kisunla has paid off.

News

FDA clears Ionis drug as first therapy for rare disease FCS

FDA clears Ionis drug as first therapy for rare disease FCS

Ionis Pharma's Tryngolza (olezarsen) has become the first FDA-approved drug therapy for adults with rare disease familial chylomicronaemia syndrome.

Editor's Picks

FDA clears first genetic hearing loss gene therapy

Trump signs order to hasten psychedelic medicine access

UK Knowledge Quarter welcomes Boehringer Ingelheim AI accelerator

UK Biobank patient data placed on sale in China

Medicare obesity drug pilot extended after insurer pushback

News

Chiesi signs $1.9bn deal to buy KalVista and its HAE drug

Chiesi signs $1.9bn deal to buy KalVista and its HAE drug

Chiesi has boosted its rare disease business with an agreement to buy KalVista and Ekterly, its oral drug for treating attacks in rare disease HAE.

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The rights of trademark owners are acknowledged. Website and content copyright © 2009-2026, pharmaphorum media limited or its licensors; all rights reserved. pharmaphorum – an EVERSANA company