spinal muscular atrophy Archives -

Zolgensma hits the ground running, says Novartis

https://pharmaphorum.com/news/zolgensma-hits-the-ground-running-says-novartis/

AveXis rules out EU compassionate use of SMA gene therapy, says Biogen option is available

https://pharmaphorum.com/news/avexis-rules-out-eu-compassionate-use-of-sma-gene-therapy-zolgensma/

Novartis in political row after denying Belgian toddler compassionate access to gene therapy

https://pharmaphorum.com/news/novartis-in-political-row-after-denying-belgian-toddler-compassionate-access-to-gene-therapy/

Weekly roundup: More questions for Novartis in Zolgensma scandal

https://pharmaphorum.com/views-and-analysis/weekly-roundup-more-questions-for-novartis-in-zolgensma-scandal/

Novartis axed Avexis execs ahead of Zolgensma scandal

https://pharmaphorum.com/news/novartis-axed-avexis-execs-ahead-of-zolgensma-scandal/

US senators blast Novartis for Zolgensma data falsification

https://pharmaphorum.com/news/us-senators-blast-novartis-for-zolgensma-data-falsification/

Second death in gene therapy trial prompts investigation

https://pharmaphorum.com/news/second-death-in-novartis-gene-therapy-trial-prompts-investigation/

PTC shares soar after SMA drug data impresses market

https://pharmaphorum.com/news/ptc-therapeutics-posts-solid-sma-data/

Biogen courts controversy with $750k-a-year rare disease drug

https://pharmaphorum.com/news/biogen-controversy/

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