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abstract shapes, bone structure, 3d render, bone

UK biotech Mereo gears up for key brittle bone drug data

UK biotech Mereo BioPharma is hoping the coming months will transform its fortunes as it prepares for potentially pivotal data for a brittle bone disease drug.

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Orphan medicines launch excellence: sustaining launch succes...

Overview Launching orphan medicines excellently will become even more important over the next five years as more patients with rare diseases have pharmacotherapies available.

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NICE backs Akcea’s Tegsedi, pipping Alnylam to hATTR okay

NICE has recommended that Akcea’s hereditary transthyretin-related amyloidosis (hATTR) treatment Tegsedi be made available on the NHS in England, ahead of a rival therapy from Alnylam.

News

Alnylam to file gene-silencing porphyria drug

Alnylam is to file its givosiran with regulators to treat a form of the blood disease porphyria, applying its gene silencing technology to the condition for the first time, following suppor

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$Banner for Media partners {460x250px}_Gene and Cell Therapy$

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Gene and Cell Therapy: Quality Developments to Commercializa...

We are pleased to invite you to the Annual Gene and Cell Therapy: Quality Developments to Commercialization Summit, scheduled for June 5-6, 2019, in Berlin, Germany.

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4th Annual Antibody Drug Conjugates (ADC) Summit: From Targe...

We are pleased to invite you to the 4th Annual Antibody Drug Conjugates Summit: From Target to Therapeutics scheduled for May 15-16, 2019 in Vienna, Austria.

UK biotech Mereo gears up for key brittle bone drug data

Orphan medicines launch excellence: sustaining launch succes...

NICE backs Akcea’s Tegsedi, pipping Alnylam to hATTR okay

Alnylam to file gene-silencing porphyria drug

Gene and Cell Therapy: Quality Developments to Commercializa...

4th Annual Antibody Drug Conjugates (ADC) Summit: From Targe...

CAR-T therapies: Faster, better, cheaper

Coming soon: The Life Sciences Industry Report 2025 – insigh...

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