Rare diseases Archives -

bluebird bio to split into oncology and gene therapy specialists

https://pharmaphorum.com/news/bluebird-bio-to-split-into-oncology-and-gene-therapy-specialists/

2020 in review: Pharma’s progress outside of COVID-19

https://pharmaphorum.com/views-analysis-oncology/2020-review-pharmas-progress-outside-of-covid-19/

Tay-Sachs and rare disease registries – the Health Heroes podcast

https://pharmaphorum.com/podcast/rare-disease-registries-kantar-health/

Operationalize: Expanded Access Programs Summit

https://pharmaphorum.com/events/operationalize-expanded-access-programs-summit/

Rocket Pharmaceuticals in orbit after gene therapy read-out

https://pharmaphorum.com/news/rocket-pharmaceuticals-shares-go-into-orbit-after-gene-therapy-read-out/

The urgent need for education and awareness about mitochondrial disease

https://pharmaphorum.com/views-and-analysis/the-urgent-need-for-education-and-awareness-about-mitochondrial-disease/

Biotech trends in COVID era: the pharmaphorum podcast

https://pharmaphorum.com/podcast/biotech-trends-pharnext-david-solomon/

‘Knowledge is power’ for rare diseases and NAbs

https://pharmaphorum.com/views-analysis-patients/knowledge-is-power-for-rare-diseases-and-nabs/

How the rare disease community has developed fertile ground for progress

https://pharmaphorum.com/views-analysis-patients/how-the-community-developed-fertile-ground-for-progress-in-rare-disease-drug-development/

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