orphan drugs

News

Orphan drugs dominate 2018 UK Prix Galien shortlist

A bumper crop of orphan drugs from the likes of Amicus, Kyowa Kirin, Eusa and Biogen dominates this year’s UK Prix Galien shortlist as biotech firms and specialist pharma companies cement t

Partner Content

Partner Content

Official Agenda released for 8th annual Orphan Drugs and Rar...

Agenda released for 8th Orphan Drugs and Rare Diseases

Events

Biosimilars_Biologics_2018_BioTech_Pharma_Summit

Partner Content

BioTech Pharma Summit: Biosimilars & Biologics 2018

Biosimilars & Biologics:The future of Biotech Medicines

News

FDA's Gottlieb vows to close orphan drug loopholes

FDA commissioner Scott Gottlieb is continuing his plans to streamline and accelerate the regulators' practices, but now plans to close down at least one glaring loophole in the Orphan Drug

Views & Analysis

Close-up shot of an old rusty key inside a keyhole

Orphan drugs: overcoming HTA barriers to access

How can orphan drug manufacturers demonstrate value and improve access to drugs?

News

Government must rethink drug rationing plans - experts

The government looks set to come under pressure to rethink moves to ration access to medicines, after a new plan from NICE and NHS England was criticised by industry representatives and oth

Orphan drugs dominate 2018 UK Prix Galien shortlist

Official Agenda released for 8th annual Orphan Drugs and Rar...

BioTech Pharma Summit: Biosimilars & Biologics 2018

FDA's Gottlieb vows to close orphan drug loopholes

Orphan drugs: overcoming HTA barriers to access

Government must rethink drug rationing plans - experts

Sanofi to buy UK vaccines developer Vicebio for $1.6bn

The value of a partner, globally and locally

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orphan drugs

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