gene editing

News

SpliceBio chief executive Miquel Vila-Perelló

SpliceBio gathers $135m for eye disease gene therapies

Spain's SpliceBio has raised $135m in financing that will help it move a gene-editing therapy for Stargardt disease through clinical testing.

News

KJ's parents, Kyle and Nicole, and his three siblings

World first as infant gets personalised CRISPR therapy

In a medical breakthrough, a child diagnosed with a rare genetic disorder has received a bespoke CRISPR gene editing therapy to correct the mutation.

News

Beam launches $500m financing on base-editing trial data

Beam says its base-editing drug has met its goals in a phase 1/2 trial in genetic disease AATD, and it wants to raise $500m to take it forward.

News

Sickle cell gene therapy Casgevy finally cleared for NHS use

Vertex's gene-editing therapy for sickle cell disease, Casgevy, has been given the nod for use by the NHS in England after an earlier rejection.

News

CRISPR biotech Intellia cuts staff as it eyes 2027 launch

Eyeing a first commercial launch in 2027, Intellia is re-prioritising by cutting 27% of its workforce and shelving a lung disease candidate.

News

Editas axes two-thirds of its staff, including its CMO

Editas Medicine ends development of its gene-editing therapy for thalassaemia and sickle cell, shedding 65% of staff and narrowing its R&D focus.

SpliceBio gathers $135m for eye disease gene therapies

World first as infant gets personalised CRISPR therapy

Beam launches $500m financing on base-editing trial data

Sickle cell gene therapy Casgevy finally cleared for NHS use

CRISPR biotech Intellia cuts staff as it eyes 2027 launch

Editas axes two-thirds of its staff, including its CMO

MSD aims to plug dengue fever vaccine gap in US

The value of a partner, globally and locally

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