Duchenne muscular dystrophy

News

Multiple studies of Sarepta's DMD therapy halted after death

Three studies of Sarepta's Elevidys Duchenne gene therapy have been placed on hold as the death of a 16-year-old boy is investigated.

News

Sarepta slumps on Elevidys patient death

The death of a patient treated with Sarepta's Duchenne muscular dystrophy gene therapy Elevidys has hit its share price.

News

Santhera's DMD drug poised for wider rollout in Germany

Santhera has agreed pricing and reimbursement for its Duchenne muscular dystrophy drug Agamree with German health funds representing 90% of patients.

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Wheelchair sign with trees in background

Santhera preps UK Duchenne drug launch after NICE says yes

Santhera will launch its new drug for Duchenne muscular dystrophy in the UK within the next few weeks after getting the green light for NHS coverage.

News

Capricor files cell therapy for DMD cardiomyopathy with FDA

Capricor completes its US filing for deramiocel, vying to become the first FDA-approved therapy for cardiomyopathy in Duchenne muscular dystrophy.

News

Price deal opens door to NHS use of Santhera DMD drug

Santhera's Duchenne muscular dystrophy (DMD) therapy Agamree has been cleared for NHS use after a confidential pricing agreement.

Multiple studies of Sarepta's DMD therapy halted after death

Sarepta slumps on Elevidys patient death

Santhera's DMD drug poised for wider rollout in Germany

Santhera preps UK Duchenne drug launch after NICE says yes

Capricor files cell therapy for DMD cardiomyopathy with FDA

Price deal opens door to NHS use of Santhera DMD drug

Ozempic patient blinded by NAION sues Novo Nordisk

Health Trends 2025: Reimagining What's Possible

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Duchenne muscular dystrophy

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