DMD Main
Group of hands holding national flags.

DMD campaigners: Advocating for change

The internet and social media are often heralded as a panacea for rare disease patients and their carers as they seek information, but for some parents it’s face-to-face collaborations and meetings

Views & Analysis
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Accelerating access for rare disease patients – the need to ...

Santhera is putting patient needs at the heart of its rare disease speciality business. Chief Executive Officer Thomas Meier, PhD, talks about the company’s mission – and how rationalising Europe’s drug review systems could help patients.

Views & Analysis
Handicap businessman discussing while sitting with colleague in creative office

Can people with Duchenne be in charge of their own lives?

Progress in health and social care in European countries is helping many boys with Duchenne muscular dystrophy (DMD) to extend their lives beyond what was once dreamed possible, and to take control of their lives as they grow up and become men.