cystic fibrosis

News

Trial of Boehringer's cystic fibrosis gene therapy imminent

Boehringer's cystic fibrosis gene therapy is poised to start clinical testing, hoping to offer a one-shot alternative to costly CFTR modulator drugs.

News

Share in cystic fibrosis firm Sionna rise sharply after IPO

Sionna has closed its IPO, raising $191m for cystic fibrosis candidates that it thinks could be more effective than rivals from Vertex.

News

Wales and NI follow England in backing Vertex CF therapies

Three of the four UK nations have agreed a long-term deal with Vertex Pharma for reimbursement of its cystic fibrosis therapies, ensuring permanent access to the drugs for eligible patients

News

Vertex’s chief executive Reshma Kewalramani

Vertex seeks swift review of new CF triple after ph3 readout

Vertex Pharma has said it will use a priority review voucher (PRV) to speed up the FDA review of its new once-daily triple therapy for cystic fibrosis, which has just hit

R&D

Partner Content

Polymer Chemistry & Formulation in Drug Delivery

Design Your Novel Polymers & Maximize Payload Compatibility for Sustained & Controlled Release

News

First Wave faces choppy waters with cystic fibrosis drug

First Wave BioPharma can’t seem to catch a break in its efforts to bring a new drug to market for pancreatic insufficiency problems that affect most patients with cystic f

Trial of Boehringer's cystic fibrosis gene therapy imminent

Share in cystic fibrosis firm Sionna rise sharply after IPO

Wales and NI follow England in backing Vertex CF therapies

Vertex seeks swift review of new CF triple after ph3 readout

Polymer Chemistry & Formulation in Drug Delivery

First Wave faces choppy waters with cystic fibrosis drug

New FDA head says no more pharma on advisory committees

Health Trends 2025: Reimagining What's Possible

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cystic fibrosis

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