Events Partner Content 2nd Gene Therapy for Blood Disorders Gene Therapy for Blood Disorders Digital Summit
News Celgene files potential blockbuster luspatercept Celgene and Acceleron Pharma have submitted their blood disorder drug luspatercept for approval with the FDA, setting up what could be a new blockbuster for the soon-to-be acquired Celgene.
News Neurogene drops high-dose arm in Rett study after death The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died
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