ATTR amyloidosis

News

Intellia shares fall after hospitalised CRISPR patient dies

Shares in gene-editing specialist Intellia Therapeutics came under renewed pressure today after a patient in one of its clinical trials died.

News

CRISPR biotech Intellia plummets as trial paused for safety

Intellia lost 45% of its value today as phase 3 trials of one of its priority drug programmes were halted due to a patient being hospitalised.

R&D

The diagnostic odyssey: Challenges and opportunities in tran...

Transthyretin amyloidosis (ATTR) is a rarely diagnosed and relentless disease that demands our attention.

News

Alnylam joins three-way contest in ATTR cardiomyopathy

Alnylam has claimed FDA approval for Amvuttra in ATTR cardiomyopathy, allowing it to compete with rival therapies from Pfizer and BridgeBio.

News

EU clears AZ, Ionis' Wainzua for ATTR polyneuropathy

AstraZeneca and Ionis add an EU green light to earlier approvals in the US and UK for ATTR polyneuropathy drug Wainzua, a potential blockbuster.

News

BridgeBio gets EU nod for ATTR cardiomyopathy drug

BridgeBio and Bayer are poised to challenge Pfizer's Vyndaqel in the EU after acoramidis gets a green light for ATTR cardiomyopathy.

Intellia shares fall after hospitalised CRISPR patient dies

CRISPR biotech Intellia plummets as trial paused for safety

The diagnostic odyssey: Challenges and opportunities in tran...

Alnylam joins three-way contest in ATTR cardiomyopathy

EU clears AZ, Ionis' Wainzua for ATTR polyneuropathy

BridgeBio gets EU nod for ATTR cardiomyopathy drug

Sofinnova Partners raises €650m for early-stage biotechs

How to meet your physicians where they are online

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ATTR amyloidosis

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