ataxia

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PTC slides on failed Friedreich ataxia study

PTC Therapeutics has cued up no fewer than three clinical trial readouts this quarter that could lead to new regulatory filings – but the latest for vatiquinone in inherit

News

Healx deploys its AI in hunt for Friedreich's ataxia therapi...

UK artificial intelligence specialist Healx has begun a partnership with two medical charities that aims to uncover new therapies for the neurodegenerative disease Friedreich's ataxia (FA).

Spotlight on

World Without Disease white paper feature image

World Without Disease initiative: 2024 update

In a new white paper from the World Without Disease initiative, a 2024 update is provided of the current endeavours and developments that have occurred since inaugural discussions last year

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Digital

The AI effect in pharma commercial strategy: From data to re...

Discover how AI is transforming the pharma commercial strategy. Unlock real-time insights & actions from data. Click here for more.

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