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Monday 29 June 2026

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APDS

News

FDA knocks back Pharming's bid for wider Joenja use

FDA knocks back Pharming's bid for wider Joenja use

The FDA has turned down Pharming's bid to broaden the label of Joenja for rare immunodeficiency disorder APDS so it can be used in younger patients.

News

Box and bottle of Joenja

First drug for rare disease APDS cleared for NHS use

Pharming's Joenja has become the first disease-modifying drug that can be used by the NHS to treat APDS, an ultra-rare immunodeficiency disorder.

News

Pharming brings first drug for rare disease APDS to US

Pharming brings first drug for rare disease APDS to US

Joenja will launch in April and could make upwards of $200m a year in sales, say analysts.

Editor's Picks

Lilly launches its LillyDirect sales channel in the UK

HHS details plan to regain the US's edge in clinical trials

Insilico and SK Bio forge $2.5bn AI neuroimmunity alliance

EFPIA report adds to pressures on EU drug pricing policy

Obesity is rising fastest in young adults in England

News

Zymeworks cuts deal to buy Theravance for $929m in cash

Zymeworks cuts deal to buy Theravance for $929m in cash

Zymeworks has reached a deal to buy Theravance, claiming rights to COPD therapy Yupelri, sold by Viatris, which made $267m last year.

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The rights of trademark owners are acknowledged. Website and content copyright © 2009-2026, pharmaphorum media limited or its licensors; all rights reserved. pharmaphorum – an EVERSANA company