Familial Chylomicronaemia Syndrome

News

Ionis, Arrowhead hail data with triglyceride drugs at ACC

Drugs from Ionis and Arrowhead Pharma that block apolipoprotein C-III (apoC-III) have shown their value in treating diseases associated with elevated triglyceride levels i

News

Ionis preps filings for olezarsen in rare disease FCS

Ionis Pharma is preparing to file for regulatory approval of its experimental therapy olezarsen for familial chylomicronaemia syndrome (FCS) in the US and Europe after the

News

NICE relents and okays Akcea’s rare disease drug Waylivra fo...

Patients with the rare disease familial chylomicronemia syndrome (FCS) will be able to access treatment with Akcea’s Waylivra via the NHS, after a U-turn by NICE.

Views & Analysis

FCS: A life-limiting condition

GP Karishma Patel tells us about the daily challenges of living with the ultra-rare condition Familial Chylomicronaemia Syndrome (FCS), which prevents the body from breaking down fats.

Ionis, Arrowhead hail data with triglyceride drugs at ACC

Ionis preps filings for olezarsen in rare disease FCS

NICE relents and okays Akcea’s rare disease drug Waylivra fo...

FCS: A life-limiting condition

Neurogene drops high-dose arm in Rett study after death

Coming soon: The Life Sciences Industry Report 2025 – insigh...

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Familial Chylomicronaemia Syndrome

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