Building our own community for an ultra-rare diseaseBo Bigelow shares the story of his daughter Tess, who has an ultra-rare genetic disorder with only 51 Share XBuilding our own community for an ultra-rare diseasehttps://pharmaphorum.com/views-and-analysis/building-our-own-community-for-an-ultra-rare-disease/
Alexion: aiming to break new ground in ultra-rare therapiesMartin Mackay, head of R&D at Alexion, talks to pharmaphorum about the company’s research pipeline for severe and Share XAlexion: aiming to break new ground in ultra-rare therapieshttps://pharmaphorum.com/articles/alexion-aiming-to-break-new-ground-in-ultra-rare-therapies/
