sickle cell disease Archives -

‘Build back better’ cannot mean longer waiting times for change

https://pharmaphorum.com/patients/covid-sickle-cell-nhs-impact/

Joy as sickle cell patients get access to Novartis’ Adakveo after NICE ruling

https://pharmaphorum.com/news/joy-as-sickle-cell-patients-get-access-to-novartis-adakveo-after-nice-ruling/

Vertex builds in gene editing yet again, with $1.2bn Arbor deal

https://pharmaphorum.com/news/vertex-builds-in-gene-editing-yet-again-with-1-2bn-arbor-deal/

MHRA grants bluebird ‘innovation passport’ for sickle cell therapy

https://pharmaphorum.com/news/mhra-grants-bluebird-innovation-passport-for-sickle-cell-therapy/

ASH: CRISPR, Vertex’ CTX001 hits the mark in red cell disorders

https://pharmaphorum.com/news/ash-crispr-vertex-ctx001-hits-the-mark-in-red-cell-disorders/

2nd Gene Therapy for Blood Disorders

https://pharmaphorum.com/events/2nd-gene-therapy-for-blood-disorders/

LentiGlobin gene therapy for sickle cell on course for filing, says bluebird

https://pharmaphorum.com/news/lentiglobin-gene-therapy-for-sickle-cell-on-course-for-filing-says-bluebird/

FDA approves Global Blood Therapeutics’ sickle cell pill

https://pharmaphorum.com/news/fda-approves-global-blood-therapeutics-sickle-cell-pill/

CRISPR trials yield encouraging data in blood disorders

https://pharmaphorum.com/news/crispr-trials-yield-encouraging-data-in-blood-disorders/

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