Rare disease drug Vimizim gets NICE ‘yes’ – but needs real-world dataNICE says it can approve BioMarin’s ultra-rare drug treatment Vimizim, but has proposed real-world data collection and a Share XRare disease drug Vimizim gets NICE ‘yes’ – but needs real-world datahttps://pharmaphorum.com/views-and-analysis/rare-disease-drug-vimizim-gets-nice-yes/