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haeomphila A

Breakthrough status for BioMarin ratchets up haemophilia A competition

Breakthrough status for BioMarin ratchets up haemophilia A competition

Andrew McConaghie BioMarin, gene therapy, haemophilia, haeomphila A, Hemophilia 0 Comment

The FDA has granted Breakthrough Therapy Designation to BioMarin’s gene therapy for haemophilia A, helping to intensify competition

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Breakthrough status for BioMarin ratchets up haemophilia A competition

https://pharmaphorum.com/news/breakthrough-status-biomarin-ratchets-haemophilia-competition/

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