News/ R&D Breakthrough status for BioMarin ratchets up haemophilia A competition Andrew McConaghie BioMarin, gene therapy, haemophilia, haeomphila A, Hemophilia 0 Comment The FDA has granted Breakthrough Therapy Designation to BioMarin’s gene therapy for haemophilia A, helping to intensify competition Share X Breakthrough status for BioMarin ratchets up haemophilia A competition https://pharmaphorum.com/news/breakthrough-status-biomarin-ratchets-haemophilia-competition/