DMD Archives -

For many years, Duchenne muscular dystrophy (DMD) was something of a forgotten disease. The boys, and some girls,

Curing DMD: Travelling together to find a meaningful destination

https://pharmaphorum.com/disease-spotlight/dmd-main/curing-dmd-travelling-together-to-find-a-meaningful-destination/

Growing concept eco Group hand children planting together on soil backgroud

Disease Spotlight/ DMD Main/ Views and analysis

Increase collaboration to widen access to DMD drugs, trials and care

louise.bellamy@pharmaphorum.com access to clinical trials, access to drugs, DMD, Duchenne muscular dystrophy 0 Comment

When it comes to fighting a rare disease like Duchenne muscular dystrophy (DMD), it’s a matter of strength

Increase collaboration to widen access to DMD drugs, trials and care

https://pharmaphorum.com/disease-spotlight/increase-collaboration-to-widen-access-to-dmd-drugs-trials-and-care/

Market Access/ Patients/ Views & Analysis/ Views & Analysis/ Views and analysis

Collaboration can ensure access to life-changing innovation

Amanda Barrell DMD, multiple sclerosis, NICE, QALY, risk sharing scheme 0 Comment

As a pioneering risk sharing scheme has shown, new medications can be the catalyst for a whole new

Collaboration can ensure access to life-changing innovation

https://pharmaphorum.com/views-analysis-market-access/access-life-changing-innovation-risk-sharing-scheme/

Disease Spotlight/ DMD Main/ Views and analysis

DMD campaigners: Advocating for change

Dominic Tyer disease, DMD, DMD campaigners, DMD campaigning, Duchenne, Klair Bayley, Parent Project Muscular Dystrophy, Pat Furlong, Ricky Andreis, Santhera, Save Our Sons, Swedish Muscular Dystrophy Research Foundation 0 Comment

The internet and social media are often heralded as a panacea for rare disease patients and their carers

DMD campaigners: Advocating for change

https://pharmaphorum.com/disease-spotlight/dmd-main/dmd-campaigners-advocating-change/

News/ Pfizer/ Rare diseases

Pfizer axes development of Duchenne muscular dystrophy antibody

Piotr Wnuk DMD, Duchenne, Duchenne muscular dystrophy, Pfizer, rare disease 0 Comment

Pfizer has axed trials of its domagrozumab antibody for Duchenne muscular dystrophy (DMD), after it failed against efficacy

Pfizer axes development of Duchenne muscular dystrophy antibody

https://pharmaphorum.com/news/duchenne-trials-axed-pfizer-dmd/

Market Access/ News/ News/ News/ R&D

Sarepta dives deeper into gene therapy

Piotr Wnuk DMD, Duchenne muscular dystrophy, Lacerta Therapeutics, Sarepta 0 Comment

Sarepta Therapeutics has handed $30 million to Lacerta in exchange for a group of gene therapies, including a

Sarepta dives deeper into gene therapy

https://pharmaphorum.com/news/sarepta-dives-deeper-gene-therapy/

Disease Spotlight/ DMD Main/ Views & Analysis

Parenting as a DMD patient

Dominic Tyer DMD, Duchenne muscular dystrophy, Mitch Coles, Muscular Dystrophy UK, Trailblazers 0 Comment

Parenting as a DMD patient The sleepless nights and steep learning curve that will be familiar to any

Parenting as a DMD patient

https://pharmaphorum.com/views-analysis-digital/parenting-as-a-dmd-patient/

Hands were a collaboration concept of teamwork

Disease Spotlight/ DMD Main/ Views and analysis

He ain’t heavy – learning about a sibling’s DMD diagnosis

Dominic Tyer DMD, DMD diagnosis, Duchenne muscular dystrophy, patient centricity, rare disease 0 Comment

It’s common for patients to want to know more about what’s causing them to be ill and their

He ain’t heavy – learning about a sibling’s DMD diagnosis

https://pharmaphorum.com/views-and-analysis/learning-sibling-dmd-diagnosis/

News/ Partner content/ Press releases

An experimental gene therapy for DMD shows positive results

Pavan Solanki diseases, DMD, Duchenne muscular dystrophy, gene therapy, neuromuscular 0 Comment

Cell & Gene Therapy 2018

An experimental gene therapy for DMD shows positive results

https://pharmaphorum.com/partner-content/an-experimental-gene-therapy-for-dmd-shows-positive-results/

Trending

DMD

Login