Curing DMD: Travelling together to find a meaningful destinationFor many years, Duchenne muscular dystrophy (DMD) was something of a forgotten disease. The boys, and some girls, Share XCuring DMD: Travelling together to find a meaningful destinationhttps://pharmaphorum.com/disease-spotlight/dmd-main/curing-dmd-travelling-together-to-find-a-meaningful-destination/
Increase collaboration to widen access to DMD drugs, trials and careWhen it comes to fighting a rare disease like Duchenne muscular dystrophy (DMD), it’s a matter of strength Share XIncrease collaboration to widen access to DMD drugs, trials and carehttps://pharmaphorum.com/disease-spotlight/increase-collaboration-to-widen-access-to-dmd-drugs-trials-and-care/
Collaboration can ensure access to life-changing innovationAs a pioneering risk sharing scheme has shown, new medications can be the catalyst for a whole new Share XCollaboration can ensure access to life-changing innovationhttps://pharmaphorum.com/views-analysis-market-access/access-life-changing-innovation-risk-sharing-scheme/
DMD campaigners: Advocating for changeThe internet and social media are often heralded as a panacea for rare disease patients and their carers Share XDMD campaigners: Advocating for changehttps://pharmaphorum.com/disease-spotlight/dmd-main/dmd-campaigners-advocating-change/
Pfizer axes development of Duchenne muscular dystrophy antibodyPfizer has axed trials of its domagrozumab antibody for Duchenne muscular dystrophy (DMD), after it failed against efficacy Share XPfizer axes development of Duchenne muscular dystrophy antibodyhttps://pharmaphorum.com/news/duchenne-trials-axed-pfizer-dmd/
Sarepta dives deeper into gene therapySarepta Therapeutics has handed $30 million to Lacerta in exchange for a group of gene therapies, including a Share XSarepta dives deeper into gene therapyhttps://pharmaphorum.com/news/sarepta-dives-deeper-gene-therapy/
Parenting as a DMD patientParenting as a DMD patient The sleepless nights and steep learning curve that will be familiar to any Share XParenting as a DMD patienthttps://pharmaphorum.com/views-analysis-digital/parenting-as-a-dmd-patient/
He ain’t heavy – learning about a sibling’s DMD diagnosisIt’s common for patients to want to know more about what’s causing them to be ill and their Share XHe ain’t heavy – learning about a sibling’s DMD diagnosishttps://pharmaphorum.com/views-and-analysis/learning-sibling-dmd-diagnosis/
An experimental gene therapy for DMD shows positive resultsCell & Gene Therapy 2018 Share XAn experimental gene therapy for DMD shows positive resultshttps://pharmaphorum.com/partner-content/an-experimental-gene-therapy-for-dmd-shows-positive-results/