DMD
Market Access/ News/ News/ Press Releases
Translarna not approved by NICE for DMD on NHS
Nicole Raleigh
ataluren, DMD, Duchenne muscular dystrophy, NICE, Translarna
0 Comment
Disease Spotlight/ DMD Main/ News/ News/ R&D
Sarepta files Duchenne muscular dystrophy gene therapy with FDA
Phil Taylor
accelerated approval, DMD, Duchenne muscular dystrophy, Sarepta
0 Comment
Disease Spotlight/ DMD Main/ Views and analysis
Curing DMD: Travelling together to find a meaningful destination
Amanda Barrell
disease, DMD, Duchenne muscular dystrophy, Duchenne Parent Project Spain, Joaquim Brites, Marisol Montolio
0 Comment
Disease Spotlight/ DMD Main/ Views and analysis
Increase collaboration to widen access to DMD drugs, trials and care
louise.bellamy@pharmaphorum.com
access to clinical trials, access to drugs, DMD, Duchenne muscular dystrophy
0 Comment
Market Access/ Patients/ Views & Analysis/ Views & Analysis/ Views and analysis
Collaboration can ensure access to life-changing innovation
Amanda Barrell
DMD, multiple sclerosis, NICE, QALY, risk sharing scheme
0 Comment
Disease Spotlight/ DMD Main/ Views and analysis
DMD campaigners: Advocating for change
Dominic Tyer
disease, DMD, DMD campaigners, DMD campaigning, Duchenne, Klair Bayley, Parent Project Muscular Dystrophy, Pat Furlong, Ricky Andreis, Santhera, Save Our Sons, Swedish Muscular Dystrophy Research Foundation
0 Comment
Pfizer axes development of Duchenne muscular dystrophy antibody
Piotr Wnuk
DMD, Duchenne, Duchenne muscular dystrophy, Pfizer, rare disease
0 Comment
Market Access/ News/ News/ News/ R&D
Sarepta dives deeper into gene therapy
Piotr Wnuk
DMD, Duchenne muscular dystrophy, Lacerta Therapeutics, Sarepta
0 Comment