Organoids: bringing life to precision medicineSwiss-based biotech QGel is hoping to offer a novel approach to precision medicine by solving several of the Share XOrganoids: bringing life to precision medicinehttps://pharmaphorum.com/r-d/views-analysis-r-d/bringing-life-precision-medicine/
Strength in numbers: Because having a rare disease isn’t rareRare doesn’t mean insignificant – in fact more people live with a rare disease than with cancer and Share XStrength in numbers: Because having a rare disease isn’t rarehttps://deep-dive.pharmaphorum.com/magazine/pharma-research-rare-diseases/global-genes-rare-diseases/
R&D Roundup: Pharma gets in on the biotech boomSome good news for the UK industry in turbulent times is always welcome, and several announcement this month Share XR&D Roundup: Pharma gets in on the biotech boomhttps://pharmaphorum.com/r-d/views-analysis-r-d/rd-roundup-pharma-gets-in-on-the-biotech-boom/
The patient perspective on advocacyGrowing up with the shadow of Huntington’s disease (HD) means Seth Rotberg understands the importance of peer support Share XThe patient perspective on advocacyhttps://deep-dive.pharmaphorum.com/magazine/pharma-research-rare-diseases/inspire-patient-advocacy-seth-rotberg/
Boosting clinical trial recruitment through patient engagementOver the years, many hands have been wrung over clinical trial recruitment – low participation rates are common Share XBoosting clinical trial recruitment through patient engagementhttps://pharmaphorum.com/views-analysis-patients/boosting-clinical-trial-recruitment-through-patient-engagement/
Harnessing RWE in rare diseasesAhead of eyeforpharma Philadelphia 2019, Sonal Bhatia, Pfizer’s vice president, North America medical lead, rare disease talked to Share XHarnessing RWE in rare diseaseshttps://pharmaphorum.com/r-d/views-analysis-r-d/harnessing-rwe-in-rare-diseases/
How pharma can support doctors who treat rare diseasesWhere do doctors see patients with rare diseases, how do they keep up with treatment advances and what Share XHow pharma can support doctors who treat rare diseaseshttps://deep-dive.pharmaphorum.com/magazine/pharma-research-rare-diseases/orphan-drug-marketing-medpanel/
Ipsen on neurotoxin research: the pharmaphorum podcastFor episode 7 of the pharmaphorum podcast I spoke to Ipsen’s Philippe Picaut about neurotoxin research, with a Share XIpsen on neurotoxin research: the pharmaphorum podcasthttps://pharmaphorum.com/podcast/ipsen-neurotoxin-research/
Living with LHON: Adapting to sight loss at 15 years oldWhen faced with a devastating diagnosis, a family has two choices – to give up or make it Share XLiving with LHON: Adapting to sight loss at 15 years oldhttps://deep-dive.pharmaphorum.com/magazine/pharma-research-rare-diseases/living-lhon-sight-loss-santhera/
